Mouse Models of Human CNTNAP1 Mutations: Strategies to Rescue and Restore Functions
January 20, 2021
Research with the Department of Cellular and Integrative Physiology UT Health San Antonio, TX
News & Stories
News from the Hereditary Neuropathy Foundation: research updates, clinical trial progress, partnerships, and advocacy wins for the Charcot-Marie-Tooth community.
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Showing 109 to 120 of 153 in News
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3 Reasons to Join the Global Registry for Inherited Neuropathies, GRIN!
January 18, 2021
What GRIN is and why you should join
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US Food and Drug Administration has agreed with Pharnext and provided clear guidance on the regulatory pathway to approval for PXT3003, including key design elements of a single pivotal Phase III study
September 15, 2020
The FDA has agreed with the key elements of Pharnext’s approach for the developmental pathway to approval for PXT3003.
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THERAPEUTIC RESEARCH IN ACCELERATED DISCOVERY (TRIAD) PROGRAM REQUEST FOR PROPOSAL GUIDELINES
September 9, 2020
The Hereditary Neuropathy Foundation (HNF) would like to advance preclinical research as quickly as possible if it aligns with our key objectives.
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Clinical Trial for CMT1A begins in Korea
July 23, 2020
Helixmith, specializing in gene therapy research for over 20 years, has kicked off its phase I and 2a clinical trial for using VM202 (Engensis) to treat CMT1A.
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Press Release: Pharnext provides regulatory and clinical update on PXT3003 Phase III study for the treatment of Charcot-Marie-Tooth Type 1A
June 10, 2020
US Food and Drug Administration has agreed with Pharnext and provided clear guidance on the regulatory pathway to approval for PXT3003, including key design elements of a single pivotal Phase III study
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10yo Addie sings her version of Try by Pink to raise awareness of CMT
January 20, 2020
Addie rewrote Try by Pink into a song about her disease and recorded it to raise awareness.
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PNS, It’s A Global Effort
November 7, 2019
Where do the top CMT researchers in the world unite to share leading-edge research? The Peripheral Nerve Society (PNS) meeting!
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HNF Presents Research Findings at Three Prestigious Conferences
November 5, 2019
Read more about the research findings presented at these conferences.
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HNF is Now Recruiting Patients for New Gene Therapy Research Projects
September 20, 2019
HNF has selected its first three types of CMT based on their potential for success…and we need your help!
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StarWise Therapeutics & HNF Form A Strategic Alliance to Bring a NextGen HDAC6 Drug Therapy to CMT2A (MFN2) Patients
December 29, 2018
HNF has been committed to funding HDAC inhibitor research since 2014.
